Amicus Therapeutics | Advancing Therapies to Treat Rare Diseases
A Rare Company

Mission-driven Innovation.

Read our Belief Statement

A Rare Company

Mission-driven Innovation.

Read our Belief Statement

A Rare Journey

Our Families are Part of the Amicus Experience.

A Rare Community

Amicus Global Research and Gene Therapy Center of Excellence in Philadelphia.

New state of the art research facility builds on the city's 250-year tradition of medical innovation.

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A Rare Commitment

To Ensuring Patient Access to Medicines.

Read more about our Expanded Access Program

A Rare Connection

We Believe In Each Other.

A Rare Approach

Diversity of Experience and Thought are Essential.

A Rare Story

Our Passion for Making a Difference Unites Us.

A Rare Dedication

We Support the Disease Communities and Their Families.

Learn more about CDKL-5 Disorder

A Rare Story

We Support the Disease Communities – and Their Families